A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new ...

A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

A baby known as KJ is the first person in the world to receive a customized CRISPR therapy designed to fix a specific mutation.

A nine-month-old baby has become the first person ever to be successfully treated with personalized gene editing therapy. Researchers corrected a specific gene mutation in baby KJ Muldoon‘s ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

An infant with a life-threatening and incurable genetic disease has become the first human to successfully receive a personalized gene editing therapy ... machinery to the baby’s liver cells ...

But half of all babies with the disorder die in the first week ... talking about gene editing and the infusions. Doctors applied a personalized treatment to cure a baby’s genetic disorder ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy ...

researchers led by teams at Children’s Hospital of Philadelphia and University of Pennsylvania report on the first use of the gene-editing technology CRISPR in a customized therapy designed to ...

The process, from diagnosis to treatment, took only six months and marks the first time the technology has been successfully ... Pennsylvania (Penn) developed the customized therapy using the gene ...

A research team supported by the National Institutes of Health (NIH) has developed and safely delivered a personalized gene editing therapy to treat ... only six months and marks the first time the ...