The FDA has granted breakthrough therapy designation to DYNE-251 for the treatment of DMD in patients amenable to exon 51 ...

A mouse model study of Precision BioSciences’ gene-editing therapy PBGENE-DMD found it produced long-term functional ...

Sarepta will soon resume shipping Elevidys for ambulatory Duchenne muscular dystrophy patients after a review of safety data ...

Del-zota was granted FDA breakthrough therapy designation for treating DMD, and its developer is on track to seek its ...

View this post on Instagram Day 2 of 30 Days of MD Topic: Being a Teenager This is Kimberly Mullis’ story: Hey fam, I’m Kimmy!! (The one in the middle:) I have SMA II, and am truly living my best ...

View this post on Instagram Day 28 of 30 Days of MD Topic: Genetics and Gardening This is @cocohollywood’s story: Lurking in my mom’s genetics is FSH muscular dystrophy (facioscapulohumeral muscular ...

Disclaimer This site is strictly a news and information website about the disease. It does not provide medical advice, diagnosis or treatment. This content is not intended to be a substitute for ...

View this post on Instagram Day 30 of 30 Days of MD Topic: Hoping for a Better Tomorrow This is Miroslava Zerova’s story: My name is Miroslava Zerova from Smolqn/ Bulgaria. l am 30 years old. I often ...

Day 25 of #30DaysOfMD Introducing Gina Salminen- I wanted to share a few things about Cannabis and Facio Scapulo Humeral Muscular Dystrophy. I was diagnosed with adult-onset Facio Scapulo Humeral ...

View this post on Instagram Day 10 of 30 Days of MD Topic: Medical Knowledge and MD This is @crystaleemarie’s story: I'm Crystal Rondeau and I have a form of MD called Spinal Muscular Atrophy Type 2.

View this post on Instagram Day 10 of #30daysofMD This is @faithabovemyability story: Topic: Faith, disability, and advocacy I was born with a type of muscular dystrophy, but 30.5 years later, I’m ...

View this post on Instagram Day 6 of #30daysofMD Introducing Brad Williams: A Scientist Tells His MD Story I first started to have muscle weakness at the age of 18. The first thing I noticed is that ...