Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...

A man born with Usher syndrome type 1b, a rare genetic disease that causes congenital deafness and progressive blindness, has ...

Europe risks ceding its leadership in rare disease innovation unless it urgently recalibrates its incentive framework, warns Enrico Piccinini, Senior Vice President EU & International at Chiesi.

The Senate Parliamentarian reversed course on a small provision in the One Big Beautiful Bill Act that could boost cures for rare diseases.

Precision BioSciences Inc., a clinical-stage company developing gene editing therapies for diseases with high unmet need, has ...

We came across a bullish thesis on Ultragenyx Pharmaceutical Inc. on Valueinvesting subreddit by bluespacecolombo. In this ...

The accountant began suffering from severe headaches during her 20s until she was diagnosed with brain arteriovenous ...

The parents of a five-year-old boy say they "constantly worry every day" because he has a rare condition, which means "there ...

Rare Disease Day is observed every year on Feb. 28 (or 29 in leap years)—the rarest day of the year, according to National Organization for Rare Disorders.

CARRIE'S RARE DISEASE "Today, I can sit here, which I think is a miracle, and not be in constant pain. I didn't have that for 19 years, I really suffered," Hodgin said.

'Rare' Disease? In the U.S., a rare disease is one that affects fewer than 200,000 people. But with around 10,000 rare diseases, that number adds up quickly.

A rare disease is classified as one that affects fewer than 200,000 people. But the sum of them looks very different: 7,000 rare diseases affect more than 30 million Americans.