News

NYC Gunman Blamed This Rare Brain Disease For His Mental Illness
From symptoms to the illness' risk factors — here’s what you need to know about the disease, which can only be detected by ...
Stories by SWNS on MSN4h
"My work stress headache was actually rare brain disease which left me paralysed"
A 'fit and healthy' woman was left paralysed after headaches she thought were 'work stress' turned out to be signs of an ...
NC Biotech3h
Precision BioSciences receives Rare Pediatric Disease and Orphan Drug designations for DMD therapy
Precision BioSciences Inc., a clinical-stage company developing gene editing therapies for diseases with high unmet need, has ...
pharmaphorum9h
Sanofi grabs Chinese rights to Arrowhead rare disease drug
The deal with Arrowhead's Visirna Therapeutics subsidiary – which also includes $265 million in milestones tied to potential ...
Laconia Daily Sun3h
Woman’s ‘work stress’ turns out to be rare brain disease
The accountant began suffering from severe headaches during her 20s until she was diagnosed with brain arteriovenous ...
Euractiv20h
Europe’s rare disease innovation progress at risk, warns senior Chiesi executive
Europe risks ceding its leadership in rare disease innovation unless it urgently recalibrates its incentive framework, warns Enrico Piccinini, Senior Vice President EU & International at Chiesi.
Chapel Hill twins diagnosed with rare disease, how family is raising awareness
Parents David and Karen Kahn took their twins to the doctor right before their 7th birthday. During the visit, their ...
Biogen Lifts Outlook As Rare Disease And Alzheimer's Drug Sales Accelerate
Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...
Medical Marketing & Media4d
Rare disease patients, caregivers are at odds over health information
The survey primarily focused on rare disease patients between the ages of 16 and 23, as well as caregivers between 25 to 55 years old. Hemophilia, albinism, cystic fibrosis and Gaucher disease were ...
PMLive6h
Biogen’s Qalsody granted MHRA approval to treat rare form of motor neurone disease
Biogen’s Qalsody (tofersen) has been approved by the Medicines and Healthcare products Regulatory Agency (MHRA) as the first ...
Mum was told son had 'happy baby syndrome' before it turned out to be rare incurable disease
British mum Laura Mattinson was devastated to learn her one-year-old son Ezra had been diagnosed with Leigh syndrome after he ...
Bizcommunity.com on MSN3d
AstraZeneca enters rare disease care in South Africa
For many rare disease patients and their families, this often results in years of uncertainty, misdiagnosis, and limited or ...