BASEL, Switzerland I June 15, 2025 I Roche (SIX: RO, ROG; OTCQX: RHHBY) announced today new dosing restrictions, effective immediately, for ELEVIDYS™ ...

After the completion of the 54th Italian-American Charity Golf Association Tournament on Saturday evening, it was time for ...

Sarepta Therapeutics on Sunday said there had been a second reported case of acute liver failure resulting in death after a patient received the company's gene therapy for a rare form of muscular ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today provided a safety ...

It's a rare genetic disorder affecting less than one percent of the population, and three-year-old Ari Knowles has it.

Eric, a beloved brother and cousin, peacefully passed away on May 25, 2025, after bravely facing the challenges of Duchenne ...

A tractor run in Keld, Swaledale has raised £5,500 for Duchenne UK, supporting research into Duchenne muscular dystrophy.

A Horsham family is battling to get hold of a drug that will slow the progress of their son's muscular dystrophy.

A tractor run in Keld, Swaledale has raised £5,500 for Duchenne UK, supporting research into Duchenne muscular dystrophy.

After two years of GP and physiotherapy appointments, Eddie's worried family finally received clarity and in April 2024 were ...