News

Managing osteoporosis and bone health in Duchenne muscular dystrophy occurs in a high-risk environment for fractures due to ...
Rare diseases, exceptional people: Filippo Buccella has battled for 25 years to improve care for children with Duchenne Muscular Dystrophy (DMD) and discover new treatments – now the fight is ...
The U.S. Food and Drug Administration ( FDA) has placed an immediate clinical hold on Sarepta Therapeutics' investigational ...
Duchenne muscular dystrophy causes muscles to deteriorate and die, only to be replaced by connective tissues and fat. It usually starts in the muscles of the legs, pelvis, and calves and ...
A Northbrook company said it has won fast-track status for approval of a drug that could become the first in the United States to treat Duchenne muscular dystrophy, a fatal muscle disease found ...
Last month Claire Ellis, aged 34, a teacher from Doncaster, set off from her home to cycle 100km in support of her son Declan ...
Sarepta Therapeutics’ Duchenne muscular dystrophy gene therapy fell short of its main Phase 3 goal, but the firm contends the full body of evidence supports expanding the therapy’s label to ...
Duchenne muscular dystrophy is rare Duchenne is a rare, progressive disorder in which muscle cells are in a constant state of destruction. Need a break? Play the USA TODAY Daily Crossword Puzzle.
Duchenne and Becker muscular dystrophy (DMD) are rare genetic diseases that cause progressive muscle breakdown. Caused by a mutation of the X-chromosome, it affects young males predominantly ...
COALITION Duchenne's 13th annual Expedition Mt Kinabalu will start tomorrow from Shangri-La's Tanjung Aru Resort and Spa, ...
The total diagnosed prevalent population of Duchenne Muscular Dystrophy (DMD) in the 7 major markets was found to be 27,685 in 2017. In case of DMD patients in the United States, the diagnosed ...
The diagnosis: muscular dystrophy. Mr. Barton turned to Google. “The first thing I read was, ‘no cure, in a wheelchair in their teens, pass in their 20s,” Mr. Barton said. “I stopped.