Transforming Preclinical Screening with Speed, Precision, and Scalability. Explore How This Model Organism is Shaping the Next Era of Pharmaceutical Innovation. Executive Summary & Key Findings Market ...

Growing up on the coast and spending time in St Lucia and Richards Bay, spotting red duikers, hippos, and crocodiles, Anban ...

Children’s Hospital of Philadelphia via AP A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

"But every day, he's showing us signs that he's growing and thriving." Researchers hope what they learn from KJ will help other rare disease patients. Gene therapies, which can be extremely ...

for newly diagnosed patients with neuronal ceroid lipofuscinosis type 2 (CLN2), a rare and life-limiting form of Batten disease. The decision is based on the treatment’s high cost—over £500,000 per ...

Just six months after a newborn at Children's Hospital of Philadelphia was diagnosed with a rare and life-threatening metabolic disorder, doctors were able to develop a personalized treatment ...

But one day, during a routine walk with his dog, he couldn't continue. 'He only lasted 10 minutes,' David said. 'That's when he knew something wasn't right.' He was diagnosed days later.

A baby born with a rare and dangerous genetic disease is thriving after receiving an experimental ... a gene therapy expert at CHOP, said. "But every day, he’s showing us signs that he’s growing and ...

Cure Rare Disease (CRD), a clinical-stage nonprofit biotechnology company developing genetic medicines for ultra-rare and rare conditions, today announced that the U.S. Food and Drug ...

Drone footage shows it off the shore of Montauk, the eastern-most point in the Hamptons, on Monday, May 12. It was captured by photographer Joanna L Steidle, who told Storyful, "I have been flying ...

Highest temperatures generally of 18C to 22C. Friday will be another dry and largely sunny day. Highest temperatures of 17C to 21C. The weekend is staying sunny and warm for the weekend.