A woman with Phenylketonuria, or PKU, now adopts kids from orphanages in China who also have it — and helps them stay healthy.

Phenylketonuria (PKU) is a rare, lifelong metabolic condition which limits a person's ability to break down protein, with devastating effects on the brain if left unmanaged[i] The Live Unlimited ...

SAN RAFAEL, Calif., Oct. 7, 2020 /PRNewswire/ -- BioMarin Pharmaceutical Inc. (Nasdaq:BMRN) today announced that the U.S. Food and Drug Administra ...

Please use one of the following formats to cite this article in your essay, paper or report: APA. Mandal, Ananya. (2023, June 12). Treatment of PKU.

BioMarin Pharmaceutical Inc. BMRN announced that the FDA has granted the company Investigational New Drug status for its gene therapy candidate, BMN 307 in patients with Phenylketonuria ("PKU"), a ...

B iotech firm PTC Therapeutics said Wednesday that its drug for phenylketonuria, or PKU, met its key goal in a Phase 3 study.. In PKU, patients’ bodies are unable to break down the amino acid ...