Preclinical data presented at Cell Symposia conference show a small molecule directed at a pathogenic RNA achieved reversal of myotonia in an animal model of myotonic dystrophy Type 1 (DM1 ...

GPCR), a clinical-stage global biopharmaceutical company developing novel oral small molecule therapeutics for metabolic diseases, today announced the selection of its lead oral small molecule ...

The new molecule targets a killer protein called BAX which kills cells by damaging mitochondria. Lead author and Dewson Lab researcher Kaiming Li said, "For the first time we could keep BAX away ...

Researchers at Maynooth University, working as part of an international team, have created a new molecule that could ... annually than HIV/AIDS or malaria. Lead researcher Luke Brennan of Maynooth ...