May 15, 2025 — A new gene editor may soon open the door to gene therapies for a wider array of ... Infant With Rare, Incurable Disease Is First to Successfully Receive Personalized Gene Therapy ...

Gene Demby is a founding member of NPRs Code Switch team, where he serves as a host of the show's podcast. In 2020, Code Switch was named Apple's inaugural Podcast Of The Year. Demby's essays for ...

Nanoscope Therapeutics is on the brink of filing for FDA approval of what could be the first gene therapy for incurable eye disease retinitis pigmentosa (RP) that can be used regardless of ...

Single-cell sequencing reveals cellular heterogeneity but is challenged by technical noise and batch effects. Here, authors present CellFM, an 800-million-parameter foundation model trained on 100 ...

May 29, 2025 — Cohesin is a protein that forms a ring-shaped complex which wraps and alters the DNA molecule shape. It moves through the DNA and creates specific loops in the genetic material ...

In another sign of the challenges facing gene therapy developers, Pfizer has abandoned its haemophilia B treatment Beqvez in all world markets, saying weak demand made the business non-viable.

Gene targeting is the process of altering a specific sequence or gene at its location in a genome. Potential modifications include deletion, insertion or replacement of endogenous sequence with ...