Rocket Pharmaceuticals shares plummeted 60% Tuesday after the firm said it halted a study of a gene-therapy drug for Danon ...

For gene therapy to work well, therapeutic molecules need to be efficiently delivered to the correct locations in the body -- a job commonly given to adeno-associated viruses (AAV). To improve the AAV ...

Readers respond to an article about gene editing and object to cuts in research funding. Also: The Covid vaccine; Senator ...

Researchers say the CRISPR-based technique used could eventually be employed to treat more people with rare genetic diseases ...

Researchers have developed a new gene therapy that can be delivered using a nasal spray, ensuring that the therapeutic is ...

Novel Gene Therapy is Addressing Both Type 1 and Type 2 Diabetes AUSTIN, Texas, May 28, 2025 /PRNewswire/ -- Genprex, Inc. (Genprex or th ...

A baby born with a rare and dangerous genetic disease is thriving after getting an experimental gene editing treatment made just for him ...

A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...

“Kelly Gene Cook Sr. Hall represents a major step toward ensuring no child is left waiting for help,” said Story. “Children ...

Stuart Haxell, a 31-year-old man from County Sligo, began losing his eyesight as a child, but after undergoing a new ...

Beghou Consulting, a leading provider of data, analytics, and technology solutions for life sciences commercialization, today announced that highly-regarded industry leaders Robert Rouse and Jason ...