Rocket Pharmaceuticals shares plummeted 60% Tuesday after the firm said it halted a study of a gene-therapy drug for Danon ...

For gene therapy to work well, therapeutic molecules need to be efficiently delivered to the correct locations in the body -- a job commonly given to adeno-associated viruses (AAV). To improve the AAV ...

Readers respond to an article about gene editing and object to cuts in research funding. Also: The Covid vaccine; Senator ...

Novel Gene Therapy is Addressing Both Type 1 and Type 2 Diabetes AUSTIN, Texas, May 28, 2025 /PRNewswire/ -- Genprex, Inc. (Genprex or th ...

Cardiovascular disease and kidney disease are two of the most urgent issues in global public health. In the United States ...

“Kelly Gene Cook Sr. Hall represents a major step toward ensuring no child is left waiting for help,” said Story. “Children ...

Stuart Haxell, a 31-year-old man from County Sligo, began losing his eyesight as a child, but after undergoing a new ...

Beghou Consulting, a leading provider of data, analytics, and technology solutions for life sciences commercialization, today announced that highly-regarded industry leaders Robert Rouse and Jason ...

Scientists have developed new tools to improve gene therapy in advanced stages of inherited retinal diseases (IRDs) such as retinitis pigmentosa and Leber congenital amaurosis.

Rui Tostoes, Chief Technology Officer at ImmuneBridge, shares how his team is redefining preclinical development and ...

Researchers engineered a new therapeutically enhanced, naturally derived particle for powerful gene therapies to tackle our ...

FDA places clinical hold of RP-A501 for the treatment of patients with Danon disease due to a patient death. Click here to ...