The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

A pivotal medical milestone has been reached. For the first time ever, researchers have used a personalized CRISPR-based gene ...

For gene therapy to work well, therapeutic molecules need to be efficiently delivered to the correct locations in the body -- a job commonly given to adeno-associated viruses (AAV). To improve the AAV ...

Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...

Rocket Pharmaceuticals shares plummeted 60% Tuesday after the firm said it halted a study of a gene-therapy drug for Danon ...

Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...

For the first time, doctors have treated an infant with a rare genetic disease with a gene-editing therapy tailored ...

Merck and Japan-based Daiichi Sankyo have withdrawn their U.S. application for an experimental lung cancer treatment after it ...

Rui Tostoes, Chief Technology Officer at ImmuneBridge, shares how his team is redefining preclinical development and ...

US researchers have engineered a novel gene therapy to target the airway and lungs via a nasal spray. For gene therapy to ...

Researchers have developed a new gene therapy that can be delivered using a nasal spray, ensuring that the therapeutic is ...