In a press release, the National Institute for Health and Care Excellence announced the first-ever approval for a ...

Stuttering can be corrected through speech therapy, and the earlier such therapy starts the better are the outcomes it ...

August marks Spinal Muscular Atrophy month. The genetic neuromuscular disease causes loss of motor neurons, which can affect muscle function. One Dallas teen is changing the perception of those who ...

Cystic fibrosis, a genetic disorder that causes severe damage to the lungs and digestive system, is another target for mRNA technology. Scientists are exploring ways to use mRNA to deliver correct ...

Breakthrough AI-powered genome editing tools now enable full chromosome manipulation—ushering in a new era of gene therapy and bioethics.

Wisconsin's chapter of the Huntington's Disease Society of America is set to host the 2025 Team Hope Walk at McKee Farms Park ...

One of the eight genetic variants "nicely overlays" a signal that was previously linked to chronic pain, a common symptom of ...

A Rhinelander family is on a mission to raise awareness and funding for research into a rare genetic disorder that affects ...

For some patients with gastrointestinal (GI) cancers like colorectal and pancreatic cancer, chemotherapy can cause severe, ...

Net loss per share (GAAP) was $0.62, but remained negative as the company continues to invest heavily in research and development. The pivotal Phase 2 trial for Danon disease was placed on clinical ...

The condition is believed to affect 67 million people worldwide — including an estimated 3.3 million Americans.

People with chronic fatigue syndrome, also known as myalgic encephalomyelitis, appear to have eight genetic signals that ...