Institutional investors including Armistice Capital, RTW Investments, and Wellington Management have increased their exposure to rare disease therapeutics companies as the orphan drugs market ...

A University of Oklahoma researcher is the first to discover that the sequence of the genetic defect in the neuromuscular disease Friedreich's ataxia isn't always as uniform as previously thought ...

A University of Oklahoma researcher is the first to discover that the sequence of the genetic defect in the neuromuscular disease Friedreich’s ataxia isn’t always as uniform as ...

Nashville comedian Fiona Cauley returns to Zanies after opening for star Nikki Glaser. Cauley laughs about her disability, smashing stereotypes.

Doctors told Mary Caruso the chances of her having a child with Friedreich's ataxia, a rare genetic disorder that affects the nervous system, were 25%. She didn’t have one child with the disease.

A 69-year-old man with a history of diffuse large B-cell lymphoma presented to the hospital with headache and ataxia. MRI showed diffuse bilateral hyperintensities on T2-weighted FLAIR images. A di ...

MM+M today revealed its 2025 MM+M Awards finalists. Now in its 22nd year, the medical marketing industry’s premier awards program returns with a new category and expansions of existing ones. The ...

The FDA is expected to decide on treatments for bronchiectasis, chronic immune thrombocytopenia, fibromyalgia, Friedreich ataxia, and recurrent respiratory papillomatosis.

Study shows aspartame affects gut microbiome and gene expression in glioblastoma, highlighting potential links to cancer progression and treatment strategies.

NEW YORK, July 07, 2025 (GLOBE NEWSWIRE) -- Lexeo Therapeutics, Inc. (Nasdaq: LXEO), a clinical stage genetic medicine company dedicated to pioneering novel treatments for cardiovascular diseases, ...

Lexeo Therapeutics' LX2006 received FDA Breakthrough Therapy designation for Friedreich ataxia, showing meaningful clinical improvements in trials.