An OU researcher has made a breakthrough discovery while studying a genetic defect. The discovery could change how the ...

Hereditary ataxias, such as Friedreich’s ataxia, are genetic, meaning they are caused by "a defect in a certain gene that is present from the start of a person’s life, inherited from your ...

Curtains up for a Cure: The Gehr family’s fight against Friedreich's Ataxia Local family host soiree to raise money and awareness about Friedreich Ataxia. Friday, June 6th 2025, 10:09 pm ...

Titled “Pharmacokinetics and Pharmacodynamics of Nomlabofusp in Non‑clinical Studies of Friedreich’s Ataxia” and “Nomlabofusp, a Fusion Protein of Human Frataxin and a Cell Penetrant ...

Biogen Netherlands has received marketing authorisation from the UK’s Medicines and Healthcare products Regulatory Agency (MHRA) for its Skyclarys (omaveloxolone) to treat Friedreich's ataxia in ...

Friedreich's Ataxia (FRDA) is a rare, inherited neurodegenerative disorder that primarily affects the nervous system and the heart. It is characterized by progressive loss of coordination and ...

Session ID: 2025-06-20:9b2e679752a5221b929c40b5 Player Element ID: vjs_video_3 ...

Lafleur, 39, lives with Friedreich ataxia, or F.A., a rare and progressive neurodegenerative disease that gradually strips away a person’s ability to control their muscles.

In the MOVE-FA long-term extension study, vatiquinone yielded a 3.7-point benefit on the modified Friedreich Ataxia Rating Scale (mFARS) at 144 weeks, as compared to a matched natural history ...

In the MOVE-FA long-term extension study (ClinicalTrials.gov Identifier: NCT05515536), results showed after 144 weeks of vatiquinone, a 3.7 point improvement was seen on the mFARS relative to a ...

Alexis Baker, living with Friedreich's Ataxia, shares her journey of perseverance, career success, and advocacy while navigating life in her 20s.