The Gher family has always had a love and a talent for the performing arts. “I really lived a pretty unaffected life until ...

The dynamics of the Friedreich's ataxia market are anticipated to change as companies across the globe work towards the ...

What Is Friedreich’s Ataxia? Friedreich’s ataxia (FA) is a rare condition. It causes damage to your nervous system that gets worse over time. As a result, you may have abnormal movements ...

SINCE Friedreich's original description 1 of 6 cases of familial hereditary ataxia in 1863, numerous papers have been written on this subject. The vast majority of these elaborate on the ...

Billionaire Graeme Hart's granddaughter Jemima Hawkesby and her friend Flynn Mitchell graduating. She is fundraising to help ...

Video content above is prompted by the following: Could you elaborate on the differential diagnosis for this disease, how it is definitively diagnosed and the impact of receiving such a diagnosis ...

About DT-216P2 DT-216P2 is an improved formulation of a GeneTAC ® small molecule designed to specifically target the GAA repeat expansion mutation that is the underlying cause of FA and restore the ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...

to treat Friedreich's ataxia in individuals aged 16 years and above. This approval was granted through a national procedure. Friedreich's ataxia is a widespread hereditary ataxia type, affecting a ...

Friedreich’s ataxia is a progressive neuromuscular disease that causes uncoordinated movement, muscle weakness, balance problems, impaired speech, and frequently, heart abnormalities.