TA-ERT is a fusion protein comprised of recombinant human NAGLU and a truncated human IGF-2 connected via an amino acid linker ... The incidence is about 100,000 and 200,000 live births. The disease ...

The company hopes to push the rare-disease treatment toward FDA approval next year. Four months after ditching its lead drug, ...

With Easter just around the corner, a host of Macon County groups are hosting Easter egg hunts and other special events.

EDEN PRAIRIE, MN / ACCESS Newswire / April 9, 2025 / Today, the Born and Schneider family announced the launch of Helen's Pink Sky Foundation, a new nonprofit dedicated to accelerating research, ...