Liver damage is a well-recognised complication of gene therapies based on adeno-associated virus (AAV) vectors, and other ...

In June 2025, Merck Sharp & Dohme LLC announced a study are to learn if people who receive intismeran autogene and ...

In JAMA, the FDA's Makary and Prasad said they will focus on modernizing review processes and lowering drug costs but don't outright mention precision medicine.

DataM Intelligence | competitive Intelligence Gene therapies, exon-skipping drugs and next-gen steroids are reshaping Duchenne muscular dys ...

Adding niraparib to abiraterone acetate and prednisone may help slow cancer growth for patients with metastatic ...

DelveInsight's Pompe Disease pipeline report depicts a robust space with 15+ active players working to develop 20+ pipeline ...

JMP Securities Silvan Tuerkcan revised the firm’s view on Taysha Gene Therapies, Inc. (NASDAQ:TSHA), raising the price target ...

BOSTON & MONTREAL, May 28, 2025--enGene Holdings Inc. (Nasdaq: ENGN or "enGene" or the "Company"), a clinical-stage, ...

The Business Research Company’s Juvenile Macular Degeneration Treatment Global Market Report 2025 – Market Size, Trends, And Forecast 2025-2034 LONDON, GREATER LONDON, UNITED KINGDOM, May 27, 2025 ...

These innovations reflect the quality and depth of our in vivo data, the power of our AI algorithms for sequence design, and our commitment to helping partners develop exceptional gene therapies ...