Time is running out for a 3-year-old Utah boy battling a rare and deadly brain disease.Kiri, the son of West Valley City ...

Precision BioSciences Inc., a clinical-stage company developing gene editing therapies for diseases with high unmet need, has ...

Justin Timberlake reveals his fight with Lyme disease. Learn prevention tips and stay safe from this rare infection in San ...

Erin Kelly is likely going to forget her eight-year-old daughter Evie’s name before her little girl finishes high school.

We came across a bullish thesis on Ultragenyx Pharmaceutical Inc. on Valueinvesting subreddit by bluespacecolombo. In this ...

Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...

The accountant began suffering from severe headaches during her 20s until she was diagnosed with brain arteriovenous ...

'Rare' Disease? In the U.S., a rare disease is one that affects fewer than 200,000 people. But with around 10,000 rare diseases, that number adds up quickly.

Europe risks ceding its leadership in rare disease innovation unless it urgently recalibrates its incentive framework, warns Enrico Piccinini, Senior Vice President EU & International at Chiesi.

For many rare disease patients, access to expert care remains out of reach. Families often endure years of misdiagnoses and medical visits before finally receiving an accurate diagnosis. This is ...

The Senate Parliamentarian reversed course on a small provision in the One Big Beautiful Bill Act that could boost cures for rare diseases.