News

Stories by SWNS on MSN5h
"My work stress headache was actually rare brain disease which left me paralysed"
A 'fit and healthy' woman was left paralysed after headaches she thought were 'work stress' turned out to be signs of an ...
NC Biotech4h
Precision BioSciences receives Rare Pediatric Disease and Orphan Drug designations for DMD therapy
Precision BioSciences Inc., a clinical-stage company developing gene editing therapies for diseases with high unmet need, has ...
pharmaphorum9h
Sanofi grabs Chinese rights to Arrowhead rare disease drug
The deal with Arrowhead's Visirna Therapeutics subsidiary – which also includes $265 million in milestones tied to potential ...
NYC Gunman Blamed This Rare Brain Disease For His Mental Illness
From symptoms to the illness' risk factors — here’s what you need to know about the disease, which can only be detected by ...
Laconia Daily Sun3h
Woman’s ‘work stress’ turns out to be rare brain disease
The accountant began suffering from severe headaches during her 20s until she was diagnosed with brain arteriovenous ...
Chapel Hill twins diagnosed with rare disease, how family is raising awareness
Parents David and Karen Kahn took their twins to the doctor right before their 7th birthday. During the visit, their ...
Biogen Lifts Outlook As Rare Disease And Alzheimer's Drug Sales Accelerate
Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...
Medical Marketing & Media4d
Rare disease patients, caregivers are at odds over health information
The survey primarily focused on rare disease patients between the ages of 16 and 23, as well as caregivers between 25 to 55 years old. Hemophilia, albinism, cystic fibrosis and Gaucher disease were ...
PMLive7h
Biogen’s Qalsody granted MHRA approval to treat rare form of motor neurone disease
Biogen’s Qalsody (tofersen) has been approved by the Medicines and Healthcare products Regulatory Agency (MHRA) as the first ...
ABC112d
Chapel Hill family starts nonprofit after twin daughters diagnosed with rare disease
CHAPEL HILL, N.C. (WTVD) -- A father and mother in Chapel Hill are sharing their painful family story to raise awareness ...
Biogen Raises Annual Profit Estimates on Strong Demand for Rare Disease Drugs
(Reuters) -Biogen raised its annual profit forecast on Thursday, betting on strong demand for its rare disease drugs such as ...
Clinical Advisor4h
Empaveli Approved for Two Rare Kidney Diseases
Pegcetacoplan inhibits C3 activation by binding to C3 and its activation fragment C3b, thereby reducing C3 glomerular fragment deposition in patients with C3G and primary IC-MPGN.