Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...

A few examples of immune checkpoint inhibitors include: Gene therapy is a way of treating diseases by editing or altering the genes within the cells of your body. In the case of cancer ...

Gene editing is already being used to treat a handful of rare genetic diseases; however, most therapies involve breaking or ...

Genetic medicines could treat certain diseases, however, the current delivery systems available—viral vectors and lipid nanoparticles (LNPs)—pose unique challenges for gene therapy applications. For ...

The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...

as many gene therapy treatments require huge numbers of fully packaged viral particles — particularly as one transitions from experimental proof-of-concept to clinical testing. For example ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder hope of a cure. Campaigners reacted with joy as health officials approved a ...

Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...

Cell and gene therapies can be life-changing for patients with certain conditions, but the process of receiving them poses barriers for patients and caregivers that require multistakeholder solutions, ...

Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.