An estimated 12,000 children are born with thalassemia major, a severe form of the disease, in India each year, accounting ...

Despite promising Phase 3 results, safety concerns, namely liver injury, have impacted Agios stock and could affect Pyrukund's approval and market adoption. Read the full report here.

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent beta-thalassemia in August 2022, and exagamglogene autotemcel (exa-cel; ...

A one-day blood donation camp for thalassemia patients was held at the Municipal Corporation office on Thursday, with the joint ...

Doctors harvest stem cells from the patient’s bone marrow and then send them off to a lab, where CRISPR is used to turn up the production of another, functional version of haemoglobin. This version is ...

Q4 2024 Earnings Call Transcript February 13, 2025 Operator: Good morning, and welcome to Agios’ Fourth Quarter 2024 ...

Dependency on future regulatory approvals for PYRUKYND and potential launches in thalassemia and sickle cell disease, which remain uncertain and could impact long-term revenue prospects.

Bluebird Bio, Inc. (NASDAQ:BLUE), on Friday, entered into a definitive agreement to be acquired by global investment firms ...

A Thalassemia screening desk has been inaugurated at the NADRA centre in Sukkur on Saturday marking a significant step ...

Meerut: A 12-bed thalassemia ward at Saharanpur district hospital now provides free treatment to nearly 145 patients, thanks to one man's relentless fight after personal tragedy. Thalassemia is an ...

In a heartwarming display of generosity, Andhra Pradesh Deputy Chief Minister Pawan Kalyan announced a substantial donation ...

Tharu tribals face higher rates of thalassemia (22-24%) and sickle cell anaemia (60%) than the general population, prompting a medical camp for 2 lakh people. The prevalence of thalassemia and ...