Charleigh Pollock, 9, is being treated for a terminal neurological disorder known as Batten disease with twice-monthly infusions of a drug that costs about $1 million per year.

Indian Prime Minister Narendra Modi has heaped praise on Trump in hopes of avoiding the additional tariffs that the new administration has slapped on other countries in its opening weeks.

The Senate has approved Trump’s most controversial picks, including Tulsi Gabbard and RFK Jr. Here’s the full list and ...

Giverny Capital Asset Management, LLC, an investment management company, recently published its fourth-quarter 2024 investor letter. A copy of the letter can be downloaded here.

February is Rare Disease Month, an annual effort to highlight the challenges families can face while navigating rare ...

Rare diseases have become an attractive target for pharmaceutical companies both on the ASX and internationally.

The FDA has made some modest efforts, but it needs an internal organization that understands and would be an aggressive ...

will host its 6th annual Rare Disease Day Saturday, February 22, 2025, from 9 a.m. to 4 p.m., at the Prince Conference Center on Calvin University’s campus. This free event will bring together people ...

these World Cancer Day quotes acknowledge the strength and perseverance that those living with the disease often draw upon, as well as their families and friends. Use one of these uplifting ...