Some children in Northern Ireland who live with a severe form of muscular dystrophy will be able to access new medication on the health service, BBC News understands. The move from the Belfast Health ...
People with Duchenne muscular dystrophy have a shorter-than-average life expectancy due to changes in muscles that affect breathing, heart activity, and other functions. However, treatment advances ...
STATEN ISLAND, N.Y. — Those who participated in “The 13th annual Michael 2025 Step For A Cure 5k Run And Walk” at the FDR Boardwalk and promenade were there to make a difference in the fight against ...
Partnership leverages AI-powered genome design to optimize AAV constructs, accelerate lead candidate selection, and improve drug substance manufacturability for rare and ultra-rare neuromuscular ...
"I don't like the attention at all," said Shep, as his family and friends call him, who gets a lot of it at school. "It just annoys me, that every day I'm asked, 'Hey, why do you need a wheelchair?' ...
MARYVILLE, Tenn. — Nine-year-old Will Leko loves Pokémon, swimming and video games. His favorite titles include Yoshi’s Crafted World and Super Mario Odyssey. But Will is also living with something ...
WALTHAM, Mass., Sept. 29, 2025 (GLOBE NEWSWIRE) -- Dyne Therapeutics, Inc. (Nasdaq: DYN), a clinical-stage company, today announced that the Ministry of Health, Labour and Welfare (MHLW) in Japan has ...
Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert analyst insights to help you invest with confidence. Satellos Bioscience ( (TSE:MSCL)) has ...