Despite these gains, access remains a major commercial hurdle. Many patients with PNH are believed to be suboptimally managed due to persistent insurance-related barriers.

Novartis has shared positive results from a phase 3b study of Fabhalta (iptacopan) in a new population of patients with the rare blood disorder paroxysmal nocturnal haemoglobinuria (PNH). The ...

In the Phase IIIB APPULSE-PNH study, adult patients with paroxysmal nocturnal hemoglobinuria (PNH) who switched to Fabhalta experienced clinically meaningful improvements in hemoglobin (Hb) levels ...

In the Phase IIIB APPULSE-PNH study, adult patients with paroxysmal nocturnal hemoglobinuria (PNH) who switched to Fabhalta experienced clinically meaningful improvements in hemoglobin (Hb) levels of ...

Clinical Study Overview and Efficacy Summary in PNH This Phase II trial was initiated following the successful completion of a Phase I study involving 40 (forty) healthy volunteers.

One Piece continues to sideline Mihawk while introducing swordsmen who may be stronger than him but what does it mean for Zoro?

It’s important to be a proactive PNH patient. You’ll want to know how to how to find a doctor and manage your treatment.

PNH treatments are better than ever before, and there’s hope they’ll continue to improve. Find out what’s in the works and how you can help.

Key considerations for transfusion requirements in patients with PNH are discussed by key opinion leaders.

Please provide a brief overview of paroxysmal nocturnal hemoglobinuria (PNH) in the United States, including its incidence and prevalence. Please explain the pathophysiology of the disease and ...

The FDA has granted Orphan Drug designation to NM5072 for the treatment of paroxysmal nocturnal hemoglobinuria (PNH).