When Nellie was diagnosed with a progressive brain disease at the age of two, Megan Gillett set out to make every moment an ...

Sarepta will soon resume shipping Elevidys for ambulatory Duchenne muscular dystrophy patients after a review of safety data ...

Robust and clinically meaningful absolute mean fetal hemoglobin (HbF) induction of 8.6% from baseline at 12 weeks of treatment; 7 of 16 patients achieved absolute HbF levels greater than 20% ― ...

Announced results from the 12 mg dose cohort (n=16) of the Phase 1b PIONEER trial of pociredir in sickle cell disease (SCD); pociredir was generally well-tolerated with no treatment-related serious ad ...

Dr Vid Karmarkar and Jitendra Chouksey, highlight why India’s ‘Sugar Boards’ must evolve into comprehensive ‘Nutrition Boards ...

Q: I wish I could go to a doctor who could outline a personalized plan for improving and protecting my health, but that’s ...

About Fulcrum Therapeutics Fulcrum Therapeutics is a clinical-stage biopharmaceutical company focused on developing small mlecules to improve the lives of patients with genetically defined rare ...

Elderly Patients, Inguinal Hernia, Treatment Options, Surgical Methods, Mesh, Non-Surgical Treatment Share and Cite: Mo, Q.Y. and Huang, Q.L. (2025) Research Progress on Treatment Options for Inguinal ...

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The European Medicines Agency determined testing failed to prove Elevidys’ benefit and issued a negative opinion that could ...

No one wants to hear the words: "You have cancer." But about 1 in 8 American women will learn they have breast cancer, according to the Centers for Disease Control and Prevention. "Breast ...