The patient, who was in a trial for a limb girdle gene therapy, is the third person to die this year after receiving a Sarepta gene therapy.

A statue made to honor veterans was stolen from a Stanchfield business, sparking a search for "Handsome Gene" and the suspects who stole him.

This is the first time such results have been achieved in both children and adult patients born with a specific type of congenital deafness.

Nicole Verdun, top gene therapy regulator at the FDA, has been forced out of the agency.

Eli Lilly will acquire gene-editing startup Verve Therapeutics for up to $1.3 billion, the companies said on Tuesday, accelerating a push into experimental cardiovascular therapies.

Leaders from the world of cell and gene therapy shared their personal stories and policy recommendations in an extraordinary roundtable conducted by the FDA in front of its recently-appointed top ...

SCARBOROUGH - Gene Griffin, 94, passed away on May 31, 2025, at the Maine Veteran’s Home with his family by his ... SCARBOROUGH – Gene Griffin, 94, passed away on May 31, 2025, at the Maine ...

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

Doctors used the gene editing tool CRISPR to treat an infant born with a rare and dangerous disease. Scientists say it could someday treat millions.

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other uncommon genetic diseases.