The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases. Doctors say they constructed a bespoke gene ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new study ...

A baby born with a rare genetic disease is "growing and thriving" after getting bespoke gene therapy. It's the first time anyone in the world has been given an experimental gene-editing treatment ...

Gene Hackman, Wes Anderson, Bill Murray on the set of 2001's 'The Royal Tenenbaums' Buena Vista Pictures/Courtesy Everett Collection Ahead of the Cannes premiere of his latest film, The Phoenician ...

Instead, KJ has made medical history. The baby, now 9 ½ months old, became the first patient of any age to have a custom gene-editing treatment, according to his doctors. He received an infusion ...

KALAMAZOO, Mich. — The family of a beloved local icon is hosting an estate sale, honoring the legacy of Gene Rhodes, most commonly known as "Gene the Pumpkin Man." Rhodes passed away last ...

They would use a technology known as CRISPR, a personalized gene-editing therapy, to find the one uniquely mutated gene out of 20,000 in his little body, and fix it. KJ subsequently received three ...

May 15, 2025 — A new gene editor may soon open the door to gene therapies for a wider array of ... Infant With Rare, Incurable Disease Is First to Successfully Receive Personalized Gene Therapy ...

A Johnson & Johnson gene therapy in development for an inherited vision-loss disorder has failed a Phase 3 study(Opens in a new window), the latest clinical research ...

The treatment, described in a new study published in The New England Journal of Medicine and presented at the American Society of Gene and Cell Therapy meeting, relies on a complex therapy known ...