Groundbreaking new research shows that it is possible to use gene therapy to restore hearing in both children and adults.

The patient, who was in a trial for a limb girdle gene therapy, is the third person to die this year after receiving a Sarepta gene therapy.

Gene therapy maker Sarepta tells FDA it won't halt shipments despite patient deaths Drugmaker Sarepta Therapeutics says it won’t comply with a request from U.S. regulators to halt all shipments ...

WASHINGTON (AP) — Drugmaker Sarepta Therapeutics said late Friday it won’t comply with a request from the Food and Drug Administration to halt all shipments of its gene therapy following the … ...

Drugmaker Sarepta Therapeutics says it won’t comply with a request from U.S. regulators to halt all shipments of its gene therapy.

Sarepta Therapeutics said on Monday it will pause all shipments of Elevidys in the United States after two teenage boys with a rare condition called Duchenne muscular dystrophy, who had received ...

The U.S. Food and Drug Administration has declined to approve Ultragenyx Pharmaceutical's experimental gene therapy to treat a rare inherited disorder, citing manufacturing concerns, the company ...