Biogen raised its annual profit forecast on Thursday, betting on strong demand for its rare disease drugs such as Skyclarys ...

Biogen Inc. (NASDAQ:BIIB) reported on Thursday that the second quarter of 2025 adjusted earnings per share were $5.47, up 4% ...

The survey primarily focused on rare disease patients between the ages of 16 and 23, as well as caregivers between 25 to 55 years old. Hemophilia, albinism, cystic fibrosis and Gaucher disease were ...

The Senate Parliamentarian reversed course on a small provision in the One Big Beautiful Bill Act that could boost cures for rare diseases.

'Rare' Disease? In the U.S., a rare disease is one that affects fewer than 200,000 people. But with around 10,000 rare diseases, that number adds up quickly.

Rare Powassan virus case in Maine highlights serious tick-borne illness with no vaccine or treatment, causing neurological symptoms and potential fatality.

Daniel Cressy yawned, tired after three days of watching a machine pull blood out of his body, extract his stem cells and ...

Scientists have corrected gene mutations in mice causing an ultra-rare disease by editing DNA directly in the brain with a ...

A rare disease is classified as one that affects fewer than 200,000 people. But the sum of them looks very different: 7,000 rare diseases affect more than 30 million Americans.

Rare Disease Day is observed every year on Feb. 28 (or 29 in leap years)—the rarest day of the year, according to National Organization for Rare Disorders.