We found that most respondents had a positive perception of gene therapy, with 37% rating their perception as ‘very positive’ ...

In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with potentially increased effectiveness and safety for the treatment of ...

Post-mortem examination of a mouse heart shows a clear delineation in blue where TREE gene enhancer sensed and responded to tissue damage of a heart attack. photo - Ken Poss Lab, Duke University ...

As a psychologist who has served as a therapist and site co-principal investigator in clinical trials of MDMA and psilocybin, I'm often asked what conditions psychedelic therapy can treat and how ...

The company behind the drug, Sarepta Therapeutics, said that the patient suffered acute liver injury, a known side effect, ...

WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for ...

HHS had argued that Vertex's plan to cover fertility services for some patients that took its gene therapy would violate anti-kickback and inducement laws.

Bharat Biotech aims to democratize gene therapies, traditionally considered prohibitively expensive and available primarily ...

Muscle-related damage and deficiencies impact a patient’s quality of life, and treatments can be limited or non-existent. Some patients find relief in physical therapy or surgery, but such ...

The NHS can now offer patients with a rare blood disorder a "transformative" new treatment after the UK's medicines watchdog gave its funding the green light. Around 200 people with haemophilia B ...