This previously untreatable genetic disorder, which affects some two to three of every 10 million newborn babies, leads to ...

Jace, 6, was born with a rare and aggressive eye condition An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain ...

Related: Gene-therapy drops restore teen's vision after genetic disease left his eyes clouded with scars The treatment was initially tested in 2018 in a small clinical trial at the Massachusetts ...