Launched in 2021, Apertura is building a next-generation gene therapy company by utilizing an integrated, machine learning-enabled, data-driven approach to improving delivery and gene expression.

In major step toward the clinic, Ring’s human viral vector delivers gene therapy to eyes of mice By Helen Floersh Apr 2, 2024 8:10am Cell & Gene Therapy Flagship Pioneering viral vectors Biotech ...

By Michael Irving July 22, 2024 Scientists have demonstrated a new gene therapy in mice that can treat muscular dystrophy, which could be ready for human use in two years Depositphotos View 1 Images ...

The first in-human trial of a CRISPR Cas system delivered by adeno-associated virus 9 gene therapy to treat HIV was able to target only the intended DNA and cleared the blood within 6 months. EBT ...

State-of-the-Art AI Predicts Gene Activity in Human Cells AI foundation model may help genetics, cancer, and complex disease research. Posted January 10, 2025 | Reviewed by Monica Vilhauer Ph.D.

New gene delivery vehicle shows promise for human brain gene therapy Date: May 16, 2024 Source: Broad Institute of MIT and Harvard Summary: In an important step toward more effective gene ...