Fanconi anemia (FA) is a rare genetic disorder impairing bone marrow's blood cell production, leading to severe health issues. Early diagnosis and tre ...

Rocket Pharmaceuticals RCKT announced that the EMA accepted the marketing authorization application (MAA), seeking approval for RP-L102, an investigational gene therapy for fanconi anemia (FA).

A recent study by researchers from Nanyang Technological University identified Fanconi anemia complementation group M (FANCM) as a crucial regulator of alternative lengthening of telomere (ALT), ...

On Thursday, the Shrewsbury and Westborough High boys' basketball teams joined up to recognize Autumn Carson, a 9-year-old girl with a Fanconi anemia.

Its clinical program is an LVV-based gene therapy for the treatment of Fanconi Anemia (FA), a difficult to treat genetic disease that leads to bone marrow failure and potentially cancer.

Schlacher K, Wu H, Jasin M. A distinct replication fork protection pathway connects Fanconi anemia tumor suppressors to RAD51-BRCA1/2. Cancer Cell 22(1):106-16, 7/2012. PMCID: PMC3954744. Siaud N, ...

Fanconi anemia (FA) is a rare genetic disorder that affects the bone marrow's ability to produce blood cells. It is aninherited condition and can cause serious health problems—including ...