Novel inhalable gene therapy trialed for people with cystic fibrosis
An inhalable medicine with the potential to improve lung disease in people with cystic fibrosis, irrespective of their ...
Boehringer Ingelheim and partners start clinical development of a first-in-class, inhaled gene therapy for people with cystic fibrosis
Boehringer Ingelheim, IP Group, the UK Respiratory Gene Therapy Consortium (GTC) 1 and OXB, 1 today announce the start of LENTICLAIR TM 1, a Phase I/II trial of BI 3720931, a novel, first-in-class, ...
Medscape2d
Novel Triple Combination Therapy May Transform Cystic Fibrosis Care in Children
Once-daily vanzacaftor-tezacaftor-deutivacaftor was safe and well-tolerated in children with cystic fibrosis, while ...
precisionmedicineonline11h
Boehringer Ingelheim Kicks Off Inhaled Cystic Fibrosis Gene Therapy Phase I/II Trial With Partners
Boehringer Ingelheim, IP Group, UK Respiratory Gene Therapy Consortium, and OXB launched the first-in-human clinical trial, known as LENTICLAIR 1.
Hosted on MSN12mon
Cystic fibrosis patient, 26, receives 3rd set of lungs after begging doc to take her case: ‘I was always told that two was it’
A 26-year-old woman with cystic fibrosis successfully received her third ... But before a match could be found, she was forced to use an oxygen tank and suffered from severe fatigue and loss ...
The Lancet8d
Patient with cystic fibrosis not diagnosed until age 23 years now treated with the new triple therapy Trikafta
The effect of cystic fibrosis on many organs and the frequent lung infections means that it is mostly diagnosed in childhood.
Medscape4y
Cystic Fibrosis Gene Therapy: Successes, Failures and Hopes for the Future
Cystic fibrosis (CF) is a single-gene disorder with ... Thus, it is not surprising that in the early years of gene therapy, CF was at the forefront of this field. Since cloning of the CF gene ...
USA Today10d
Everything to know about cystic fibrosis and what causes it
The genetic disorder cystic fibrosis is unique because it can cause both breathing and digestive problems. Some 40,000 people in the U.S. currently have it, "though this is likely an ...
EurekAlert!1d
Novel inhalable gene therapy trialled for people with cystic fibrosis
An inhalable medicine with the potential to improve lung disease in people with cystic fibrosis, irrespective of their mutation type, is being tested in human trials in the UK and Europe.