The drug, Givinostat, has been approved as safe for use but Belfast Health Trust, NI's specialist centre for the condition, ...

Participants with Duchenne muscular dystrophy (DMD) who received RGX-202 demonstrated functional improvement and better ...

U.S. FDA successfully completed Pre-License Inspection; Company expects facility will meet all requirements to support ...

Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the ...

Parents of children with an incurable muscle-wasting condition have called on the Minister for Health to accelerate the ...

A Horsham family is battling to get hold of a drug that will slow the progress of their son's muscular dystrophy.

Capricor Therapeutics' rating was downgraded amid FDA inspection risks, regulatory uncertainty, and potential delays in ...

Eric, a beloved brother and cousin, peacefully passed away on May 25, 2025, after bravely facing the challenges of Duchenne ...

The parents of a nine-year-old boy battling a devastating muscle-wasting condition say new research could offer them more ...

A tractor run in Keld, Swaledale has raised £5,500 for Duchenne UK, supporting research into Duchenne muscular dystrophy.

Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the deterioration of skeletal muscle in the disease. The use of cardiac ...